The Rising Potential of the Mucopolysaccharidosis I Drugs Market Mucopolysaccharidosis I (MPS I) is a rare hereditary disorder caused by the deficiency of the α-L-iduronidase enzyme. This enzyme shortage results in the accumulation of glycosaminoglycans (GAGs) within cells, progressively damaging various organs and systems. Consequently, individuals with MPS I often experience skeletal abnormalities, respiratory complications, vision and hearing...
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